Meeting the Unique Challenges of Orphan Drug Development

While individually rare, orphan diseases are actually collectively common, with an estimated 350 million sufferers worldwide. Since the introduction of the US Orphan Drug Act more than 30 years ago, the number of orphan designations has skyrocketed and experts are predicting worldwide sales of drug will reach $176 billion by the end of 2020.

 
 
(Click to Enlarge Pages)